Posted inAutoimmune Diseases, New Drugs, Rare/Orphan Diseases, Regulatory Empaveli: Powerful New Drug for Paroxysmal Nocturnal Hemoglobinuria by Tanya von Reuss and Alex Avisoni May 20, 2021September 8, 2022 Pegcetacoplan is more effective in treating paroxysmal nocturnal hemoglobinuria compared to Soliris.